DB-OTO Gene Therapy for Inherited Deafness.
Vassili Valayannopoulos 1 , Manohar Bance 2 , Daniela S Carvalho 3 , John H Greinwald Jr 4 , Steven A Harvey 5 , Akira Ishiyama 6 , Evie C Landry 7 , Hubert Löwenheim 8 , Lawrence R Lustig 9 , Manuel Manrique 10 , Robert Nash 11 , Rubén Polo 12 , Cedric V Pritchett 13 , Jay T Rubinstein 14 , A Eliot Shearer 15 , Ignacio Del Castillo 16 17 , Jeffery J Anderson 1 , C Eduardo Corrales 1 18 , Tera M Quigley 1 , William J Riggs 1 , Peter Weber 1 , Gary Wilson 1 , Susan C Irvin 1 , Hazem E Hassan 1 , Yanping Chen 1 , Rong Liu 1 , Meghan C Drummond 1 , Leah R Sabin 1 , Bret J Musser 1 , George D Yancopoulos 1 , Christos A Kyratsous 1 , Gary A Herman 1 , Aris Baras 1 , Jonathon P Whitton 1 ; CHORD Study Group
N Engl J Med. 2025 Oct 12.
DOI: 10.1056/NEJMoa2400521